Genethon
Clinical trials sponsored by Genethon, explained in plain language.
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Gene therapy trial offers hope for boys with rare immune disorder
Disease control TerminatedThis study tested a gene therapy for boys with X-linked chronic granulomatous disease (X-CGD), a rare condition where white blood cells cannot kill bacteria and fungi, leading to severe infections. The treatment involved taking the patients' own blood stem cells, adding a working…
Phase: PHASE1, PHASE2 • Sponsor: Genethon • Aim: Disease control
Last updated May 26, 2026 06:12 UTC
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Gene therapy trial offers hope for boys with rare immune disease
Disease control TerminatedThis study tested a gene therapy for boys with X-linked chronic granulomatous disease (X-CGD), a rare disorder where white blood cells cannot fight infections. The treatment involved taking the patient's own blood stem cells, adding a corrected gene, and returning them to the bod…
Phase: PHASE1, PHASE2 • Sponsor: Genethon • Aim: Disease control
Last updated May 19, 2026 11:47 UTC