Emily De Los Reyes
Clinical trials sponsored by Emily De Los Reyes, explained in plain language.
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First gene therapy attempt for rare brain disorder begins
Disease control ENROLLING_BY_INVITATIONThis study tests a new gene therapy for people with SLC6A1 neurodevelopmental disorder, a rare genetic condition that affects brain function. One participant will receive a single injection of a harmless virus carrying a working copy of the SLC6A1 gene into the spinal fluid. The …
Phase: PHASE1, PHASE2 • Sponsor: Emily de los Reyes • Aim: Disease control
Last updated May 26, 2026 11:09 UTC
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Gene therapy survivors tracked for years in rare brain disease study
Knowledge-focused OngoingThis study follows 10 people with CLN6 Batten disease who previously received a one-time gene therapy injection into the spine. Researchers are checking for long-term side effects and using a standard scale to measure how the disease progresses over time. The goal is to understan…
Sponsor: Emily de los Reyes • Aim: Knowledge-focused
Last updated May 18, 2026 12:13 UTC