Emily De Los Reyes
Clinical trials sponsored by Emily De Los Reyes, explained in plain language.
Upcoming readouts
Trials from this sponsor expected to report results within the next 12 months.
- Gene therapy for rare brain disease tracked over years Results expected Dec 2026 (estimated)
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Gene therapy for rare brain disease tracked over years
Disease control OngoingThis study follows 10 people with CLN6 Batten disease who received a single dose of gene therapy (AT-GTX-501) in an earlier trial. Researchers are checking long-term safety and how the disease progresses over time. No new treatment is given in this follow-up.
Sponsor: Emily de los Reyes • Aim: Disease control
Last updated Jun 27, 2026 07:52 UTC
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First gene therapy injection targets rare brain disorder
Disease control By invitation onlyThis early-phase trial tests a one-time gene therapy injection into the spinal fluid for people with SLC6A1 neurodevelopmental disorder, a rare genetic condition. The study involves just 1 participant and will monitor safety and changes in behavior and development over 3 years. T…
Phase 1/2 • Sponsor: Emily de los Reyes • Aim: Disease control
Last updated Jun 26, 2026 17:08 UTC