Csl Behring

This study tested a single infusion of gene therapy (AMT-061) in 67 adults with severe or moderately severe hemophilia B. The treatment delivers a working copy of the factor IX gene to the liver, aiming to reduce bleeding episodes and the need for regular factor IX infusions. Res…

This study tested a monthly injection called Garadacimab to prevent swelling attacks in children aged 2 to 11 with hereditary angioedema (HAE). The goal was to see if the drug is safe and reduces how often attacks happen. 22 children took part, and researchers tracked side effect…

This study tested a monthly injection called Garadacimab to prevent painful swelling attacks in people with hereditary angioedema (HAE). 171 people aged 12 and older took part. The goal was to see if the drug is safe and effective over the long term. Results showed it can greatly…

This study tested whether a protein called alpha-1 antitrypsin can prevent graft-versus-host disease (GVHD) in people receiving a blood stem cell transplant for blood cancers like leukemia or lymphoma. GVHD happens when donor immune cells attack the patient's body. The trial incl…

This early-stage study tested a new drug, CSL040, in 62 healthy adults to see if it is safe and how the body processes it. The goal is to gather information for future studies in people with immune system disorders. No treatment benefit was expected for participants.

This study looked at how taking vamifeport with or without food changes the amount of drug in the blood. It involved 28 healthy adults aged 18 to 60. The goal was to understand the drug's absorption, not to treat any disease.