Den här översättningen är inte klar ännu. Den här sidan är just nu på engelska.

Gå till den engelska sidan

Cure My Disease

Don't miss your cure!

Log in / Sign up

← Back to home

Beyond Batten Disease Foundation

Clinical trials sponsored by Beyond Batten Disease Foundation, explained in plain language.

Experimental drug tested for rare brain disease in adults

Disease control Completed

This study tested whether an oral drug called miglustat is safe and might help control symptoms in adults with CLN3 Batten disease, a rare genetic disorder that affects the brain. Six participants aged 17 and older took the drug daily for two years while researchers monitored sid…

Phase: PHASE1, PHASE2 • Sponsor: Beyond Batten Disease Foundation • Aim: Disease control

Last updated Apr 03, 2026 14:42 UTC