Akouos, Inc.
Clinical trials sponsored by Akouos, Inc., explained in plain language.
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Gene therapy for inherited deafness: long-term safety check begins
Disease control ENROLLING_BY_INVITATIONThis study checks the long-term safety and effectiveness of a gene therapy called AAVAnc80-hOTOF in 30 people with hearing loss due to otoferlin gene mutations. All participants previously received the therapy in an earlier trial. Researchers will watch for late side effects and …
Sponsor: Akouos, Inc. • Aim: Disease control
Last updated May 26, 2026 07:48 UTC
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Gene therapy watch: 100 patients tracked for Long-Term safety and tumor control
Disease control ENROLLING_BY_INVITATIONThis study follows about 100 people with vestibular schwannoma (a non-cancerous brain tumor) who previously received a gene therapy called AAVAnc80-antiVEGF. Researchers will monitor participants for years to check for late side effects and measure any changes in tumor size using…
Sponsor: Akouos, Inc. • Aim: Disease control
Last updated May 22, 2026 14:03 UTC