Agios Pharmaceuticals, Inc.
Clinical trials sponsored by Agios Pharmaceuticals, Inc., explained in plain language.
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Could this pill boost hemoglobin in kids with thalassemia?
Disease control Not yet recruitingThis study tests a drug called mitapivat in children aged 1 to 17 with a type of thalassemia that does not require regular blood transfusions. The goal is to see if the drug can raise hemoglobin levels and improve anemia compared to a placebo. About 45 children will take part in …
Phase: PHASE3 • Sponsor: Agios Pharmaceuticals, Inc. • Aim: Disease control
Last updated May 26, 2026 08:31 UTC
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Could a pill cut transfusions for kids with thalassemia?
Disease control Not yet recruitingThis study tests an experimental drug called mitapivat in children aged 1 to 17 with transfusion-dependent thalassemia, a blood disorder requiring regular red blood cell transfusions. The goal is to see if mitapivat can safely reduce the number of transfusions needed compared to …
Phase: PHASE3 • Sponsor: Agios Pharmaceuticals, Inc. • Aim: Disease control
Last updated May 22, 2026 13:52 UTC