X-LINKED ADRENOLEUKODYSTROPHY
Clinical trials for X-LINKED ADRENOLEUKODYSTROPHY explained in plain language.
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New gene therapy trial offers hope for rare brain disease
Disease control Recruiting nowThis study tests a new gene therapy for X-linked adrenoleukodystrophy (X-ALD), a rare genetic disorder that damages the brain. The therapy uses a modified virus to deliver a working copy of the faulty gene directly into the spinal fluid and bloodstream. The goal is to slow or sto…
Matched conditions: X-LINKED ADRENOLEUKODYSTROPHY
Phase: NA • Sponsor: Shenzhen Geno-Immune Medical Institute • Aim: Disease control
Last updated May 12, 2026 13:43 UTC
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Massive leukodystrophy biobank aims to unlock secrets of rare brain diseases
Knowledge-focused Recruiting nowThis study is creating a large collection of medical data and biological samples from people with leukodystrophies—rare disorders that damage the brain's white matter. Researchers will use this information to discover new genetic causes, develop better diagnostic tools, and track…
Matched conditions: X-LINKED ADRENOLEUKODYSTROPHY
Sponsor: Children's Hospital of Philadelphia • Aim: Knowledge-focused
Last updated May 26, 2026 09:32 UTC