Wilsons disease
Clinical trials for Wilsons disease explained in plain language.
Never miss a new study
Get alerted when new Wilsons disease trials appear
Sign up with your email to follow new studies for Wilsons disease, keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.
Genom att skicka in godkänner du våra Användarvillkor
-
Can a single infusion rewrite the genetic code behind wilson disease?
Cure Recruiting nowThis trial tests an experimental therapy called PM577a, which uses prime editing to correct a common genetic mutation that causes Wilson disease. The treatment is given as a single intravenous infusion and aims to restore the liver's ability to remove excess copper. The study inc…
Matched conditions: WILSONS DISEASE
Phase 1/2 • Sponsor: Prime Medicine, Inc. • Aim: Cure
Last updated Sep 17, 2026 00:00 UTC
-
MRNA therapy hopes to fix copper problem in wilson disease
Disease control Recruiting nowThis early-phase trial tests a new mRNA drug called DSL101 in 18 adults with Wilson disease, a genetic condition that causes copper buildup. The drug is designed to help the body produce a protein that controls copper. Participants receive low, medium, or high doses by IV every f…
Matched conditions: WILSONS DISEASE
Early phase 1 • Sponsor: DSciLab Co., Ltd. • Aim: Disease control
Last updated Jun 27, 2026 08:13 UTC