Transfusion dependent beta-thalassaemia

Clinical trials for Transfusion dependent beta-thalassaemia explained in plain language.

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Trials to join now! 1 Completed 1

Gene editing could cure sickle cell and thalassemia in new trial

Cure Recruiting now

This early-stage trial tests a gene-editing treatment for people with severe sickle cell disease or beta-thalassemia. The approach uses the patient's own blood stem cells, which are edited to boost fetal hemoglobin—a healthy type that can replace the defective hemoglobin. Up to 1…

Matched conditions: TRANSFUSION DEPENDENT BETA-THALASSAEMIA

Phase 1 • Sponsor: Daniel Bauer • Aim: Cure

Last updated Jun 27, 2026 09:01 UTC

Transfusion dependent beta-thalassaemia

Get alerted when new Transfusion dependent beta-thalassaemia trials appear

Gene editing could cure sickle cell and thalassemia in new trial