TRANSFUSION DEPENDENT BETA-THALASSAEMIA

Clinical trials for TRANSFUSION DEPENDENT BETA-THALASSAEMIA explained in plain language.

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Trials to join now! 1 Completed 1

One-Time gene edit aims to cure devastating blood diseases

⭐️ CURE ⭐️ Recruiting now

This early-stage trial is testing a one-time gene editing treatment for people with severe sickle cell disease or beta-thalassemia. Doctors take a patient's own blood stem cells, edit a specific gene to boost healthy fetal hemoglobin, and return the cells after chemotherapy. The …

Matched conditions: TRANSFUSION DEPENDENT BETA-THALASSAEMIA

Phase: PHASE1 • Sponsor: Daniel Bauer • Aim: ⭐️ CURE ⭐️

Last updated Mar 27, 2026 12:38 UTC

TRANSFUSION DEPENDENT BETA-THALASSAEMIA

Get alerted when new TRANSFUSION DEPENDENT BETA-THALASSAEMIA trials appear

One-Time gene edit aims to cure devastating blood diseases