TRANSFUSION-DEPENDENT ALPHA-THALASSEMIA

Clinical trials for TRANSFUSION-DEPENDENT ALPHA-THALASSEMIA explained in plain language.

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Pill aims to free patients from constant blood transfusions

Disease control Ongoing

This Phase 3 trial tested whether an oral medication called mitapivat could reduce the need for regular blood transfusions in adults with severe forms of thalassemia. 258 participants who required frequent transfusions were randomly assigned to receive either mitapivat or a place…

Matched conditions: TRANSFUSION-DEPENDENT ALPHA-THALASSEMIA

Phase: PHASE3 • Sponsor: Agios Pharmaceuticals, Inc. • Aim: Disease control

Last updated Apr 01, 2026 14:41 UTC

TRANSFUSION-DEPENDENT ALPHA-THALASSEMIA

Get alerted when new TRANSFUSION-DEPENDENT ALPHA-THALASSEMIA trials appear

Pill aims to free patients from constant blood transfusions