POMPE DISEASE (LATE-ONSET)
Clinical trials for POMPE DISEASE (LATE-ONSET) explained in plain language.
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Gene therapy shot could free pompe patients from weekly infusions
Disease control Recruiting nowThis early-stage trial is testing a single intravenous dose of a gene therapy called AB-1009 in 12 adults with late-onset Pompe disease. Participants must have been on standard enzyme replacement therapy for at least 6 months. The main goal is to check safety and see if the treat…
Matched conditions: POMPE DISEASE (LATE-ONSET)
Phase: PHASE1, PHASE2 • Sponsor: AskBio Inc • Aim: Disease control
Last updated May 22, 2026 13:54 UTC
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Could electrical shocks help weak muscles? new study hopes to find out
Symptom relief Recruiting nowThis study is testing whether whole-body electrical muscle stimulation (WB-EMS) can help adults with neuromuscular diseases like ALS, muscular dystrophy, and myasthenia gravis exercise safely. Because these conditions make normal exercise difficult, WB-EMS uses electrical pulses …
Matched conditions: POMPE DISEASE (LATE-ONSET)
Phase: NA • Sponsor: University of Missouri-Columbia • Aim: Symptom relief
Last updated May 26, 2026 04:53 UTC
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New study monitors pregnancy in pompe disease patients
Knowledge-focused Recruiting nowThis study follows pregnant women with Pompe disease to see how their condition and treatments affect pregnancy and baby growth. About 20 women will join, and their babies will be checked for up to 3 years after birth. No new treatments are tested—only standard care is given.
Matched conditions: POMPE DISEASE (LATE-ONSET)
Sponsor: Genzyme, a Sanofi Company • Aim: Knowledge-focused
Last updated May 26, 2026 04:37 UTC