POMPE DISEASE LATE-ONSET
Clinical trials for POMPE DISEASE LATE-ONSET explained in plain language.
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One-Time gene therapy could change pompe disease treatment
Disease control Recruiting nowThis study tests a single intravenous dose of a gene therapy called AB-1009 in 12 adults with late-onset Pompe disease. Participants must have been on enzyme replacement therapy for at least 6 months. The main goal is to check safety and side effects, while also seeing if the tre…
Matched conditions: POMPE DISEASE LATE-ONSET
Phase: PHASE1, PHASE2 • Sponsor: AskBio Inc • Aim: Disease control
Last updated Jun 27, 2026 12:38 UTC
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Shocking muscles to move: new exercise hope for nerve disease patients
Symptom relief Recruiting nowThis study tests whether whole-body electrical muscle stimulation (WB-EMS) can help adults with neuromuscular diseases like ALS, SMA, and muscular dystrophy exercise safely. Because these conditions weaken the nerves that control muscles, traditional exercise is often too hard. W…
Matched conditions: POMPE DISEASE LATE-ONSET
Phase: NA • Sponsor: University of Missouri-Columbia • Aim: Symptom relief
Last updated Jun 27, 2026 11:03 UTC
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New study monitors pregnancy in pompe disease patients
Knowledge-focused Recruiting nowThis study follows pregnant women with Pompe disease to see how the condition and its treatments affect pregnancy and infant growth. Researchers will track complications and monitor babies for up to three years after birth. No new drugs are being tested; participants receive thei…
Matched conditions: POMPE DISEASE LATE-ONSET
Sponsor: Genzyme, a Sanofi Company • Aim: Knowledge-focused
Last updated Jun 27, 2026 12:07 UTC