PMM2-CDG
Clinical trials for PMM2-CDG explained in plain language.
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Hope for rare disease: new drug shows promise in Long-Term study
Disease control By invitation onlyThis study is for people with PMM2-CDG, a rare genetic disorder, who have already taken the experimental drug GLM101 in a previous trial. The goal is to see if GLM101 is safe and effective over a longer period. Participants will receive weekly infusions of GLM101 at the same dose…
Matched conditions: PMM2-CDG
Phase 2 • Sponsor: Glycomine, Inc. • Aim: Disease control
Last updated Sep 17, 2026 00:00 UTC
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Experimental drug GLM101 targets rare PMM2-CDG in pivotal trial
Disease control OngoingThis study tests a drug called GLM101 for people with PMM2-CDG, a rare inherited disease that affects movement and coordination. About 50 children and adults will receive weekly infusions of either GLM101 or a placebo for 24 weeks, followed by an open-label phase where everyone g…
Matched conditions: PMM2-CDG
Phase 2/3 • Sponsor: Glycomine, Inc. • Aim: Disease control
Last updated Aug 16, 2026 00:00 UTC