PAROXYSMAL NOCTURNAL HEMOGLOBINURIA
Clinical trials for PAROXYSMAL NOCTURNAL HEMOGLOBINURIA explained in plain language.
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PNH drug safety study ends early
Disease control TerminatedThis study was for people with paroxysmal nocturnal hemoglobinuria (PNH) who had already been helped by the drug BCX9930 in an earlier study. The goal was to keep giving them the drug and watch for side effects over time. The study was stopped early, and only 28 people took part.
Matched conditions: PAROXYSMAL NOCTURNAL HEMOGLOBINURIA
Phase: PHASE2 • Sponsor: BioCryst Pharmaceuticals • Aim: Disease control
Last updated May 26, 2026 09:07 UTC
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Real-World check: does iptacopan help PNH patients in russia?
Disease control TerminatedThis study followed 6 adults with PNH who were already taking iptacopan as part of their normal care in Russia. Researchers tracked whether their hemoglobin levels improved and if they needed fewer blood transfusions over 6 to 12 months. The study was stopped early, so results ar…
Matched conditions: PAROXYSMAL NOCTURNAL HEMOGLOBINURIA
Sponsor: Novartis Pharmaceuticals • Aim: Disease control
Last updated May 20, 2026 11:55 UTC