NEURODEGENERATIVE DISEASE, HEREDITARY
Clinical trials for NEURODEGENERATIVE DISEASE, HEREDITARY explained in plain language.
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One-shot gene therapy aims to stop rare nerve disease in its tracks
Disease control Recruiting nowThis study tests a single dose of a gene therapy called NTLA-2001 in 60 people with a rare inherited nerve disease (ATTRv-PN). The goal is to see if it can safely reduce harmful protein buildup and slow nerve damage compared to a placebo. Participants must have a confirmed diagno…
Matched conditions: NEURODEGENERATIVE DISEASE, HEREDITARY
Phase: PHASE3 • Sponsor: Intellia Therapeutics • Aim: Disease control
Last updated May 22, 2026 14:01 UTC
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Scientists hunt for Parkinson's clues with advanced brain scans
Knowledge-focused Recruiting nowThis study aims to find a biological marker for Parkinson's disease by using special brain scans (PET, SPECT, and MRI) in 45 people with certain genetic mutations. The goal is to better understand brain changes in Parkinson's and help develop new medications that could slow the d…
Matched conditions: NEURODEGENERATIVE DISEASE, HEREDITARY
Sponsor: University of Exeter • Aim: Knowledge-focused
Last updated May 19, 2026 11:48 UTC