MUSCULAR DYSTROPHIES
Clinical trials for MUSCULAR DYSTROPHIES explained in plain language.
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Cell therapy shows promise in slowing duchenne muscular dystrophy
Disease control OngoingThis study tests a cell therapy called deramiocel (CAP-1002) in 106 boys and young men with Duchenne muscular dystrophy (DMD), a genetic disease that weakens muscles over time. Participants receive either deramiocel or a placebo every 3 months for a year, then all can receive der…
Matched conditions: MUSCULAR DYSTROPHIES
Phase: PHASE3 • Sponsor: Capricor Inc. • Aim: Disease control
Last updated May 26, 2026 05:06 UTC
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New hope for FSHD: Long-Term drug safety trial underway
Disease control OngoingThis study looks at the long-term safety and effectiveness of a drug called AOC 1020 for people with FSHD, a genetic disease that causes muscle weakness. About 84 adults who completed a previous study will receive the drug through an IV. The main goal is to check for side effects…
Matched conditions: MUSCULAR DYSTROPHIES
Phase: PHASE2 • Sponsor: Avidity Biosciences, Inc. • Aim: Disease control
Last updated May 18, 2026 12:08 UTC
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New model aims to speed up rare disease diagnoses
Knowledge-focused OngoingThis study is testing a new way to care for people with rare diseases. It brings together specialists, advanced lab tests, and better data sharing to help diagnose patients faster and improve their overall care. The study involves 136 participants with conditions like mitochondri…
Matched conditions: MUSCULAR DYSTROPHIES
Sponsor: Fondazione Policlinico Universitario Agostino Gemelli IRCCS • Aim: Knowledge-focused
Last updated May 26, 2026 04:35 UTC
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Massive study aims to unlock secrets of childhood nerve and muscle diseases
Knowledge-focused OngoingThis study looks at people with inherited nerve and muscle disorders that begin in childhood, along with their family members and healthy volunteers. The goal is to better understand how these diseases progress over time and to find better ways to measure changes in patients. Res…
Matched conditions: MUSCULAR DYSTROPHIES
Sponsor: National Institute of Neurological Disorders and Stroke (NINDS) • Aim: Knowledge-focused
Last updated May 22, 2026 14:03 UTC