METHYLMALONIC ACIDEMIA
Clinical trials for METHYLMALONIC ACIDEMIA explained in plain language.
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Extended trial tests promising genetic disorder therapy
Disease control Recruiting nowThis study follows patients with methylmalonic acidemia (MMA), a rare genetic disorder, who have already received the experimental treatment mRNA-3705 in earlier trials. The goal is to monitor the long-term safety and effectiveness of continued treatment. Participants will receiv…
Matched conditions: METHYLMALONIC ACIDEMIA
Phase: PHASE1, PHASE2 • Sponsor: ModernaTX, Inc. • Aim: Disease control
Last updated Apr 04, 2026 01:51 UTC
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Landmark study seeks to unlock mysteries of rare metabolic disease
Knowledge-focused Recruiting nowThis study aims to better understand methylmalonic acidemia (MMA), a rare and serious inherited metabolic disorder. Researchers will observe over 2,000 patients to learn how the disease progresses, identify complications, and find biological markers. The goal is to gather essenti…
Matched conditions: METHYLMALONIC ACIDEMIA
Sponsor: National Human Genome Research Institute (NHGRI) • Aim: Knowledge-focused
Last updated Mar 11, 2026 14:54 UTC