METHYLMALONIC ACIDEMIA
Clinical trials for METHYLMALONIC ACIDEMIA explained in plain language.
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New mRNA therapy for rare metabolic disease moves to Long-Term safety check
Disease control Recruiting nowThis study looks at the long-term safety of an experimental mRNA treatment called mRNA-3705 for people with methylmalonic acidemia (MMA), a rare genetic disorder. Participants have already taken part in earlier studies of this drug. Researchers will monitor side effects and measu…
Matched conditions: METHYLMALONIC ACIDEMIA
Phase: PHASE1, PHASE2 • Sponsor: ModernaTX, Inc. • Aim: Disease control
Last updated May 26, 2026 11:54 UTC
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NIH launches Long-Term study to unlock mysteries of rare metabolic disease
Knowledge-focused Recruiting nowThis study aims to learn more about methylmalonic acidemia (MMA), a rare genetic disorder that affects how the body processes certain proteins and fats. Researchers will observe up to 2,275 participants over time, using tests like blood draws, imaging, and developmental assessmen…
Matched conditions: METHYLMALONIC ACIDEMIA
Sponsor: National Human Genome Research Institute (NHGRI) • Aim: Knowledge-focused
Last updated May 26, 2026 11:54 UTC