MEDIUM-CHAIN ACYL-COA DEHYDROGENASE DEFICIENCY
Clinical trials for MEDIUM-CHAIN ACYL-COA DEHYDROGENASE DEFICIENCY explained in plain language.
Never miss a new study
Get alerted when new MEDIUM-CHAIN ACYL-COA DEHYDROGENASE DEFICIENCY trials appear
Sign up with your email to follow new studies for MEDIUM-CHAIN ACYL-COA DEHYDROGENASE DEFICIENCY, keep track of the ones that matter, and come back to a personal dashboard instead of checking manually.
Genom att skicka in godkänner du våra Användarvillkor
-
Could a liver drug help people with MCADD fast safely?
Disease control TerminatedThis study tests whether sodium phenylbutyrate, a drug already approved for another condition, can help people with MCAD deficiency—a genetic disorder that makes it hard to break down fats for energy. About 24 participants aged 10 and older will take the drug for 4 weeks. Researc…
Matched conditions: MEDIUM-CHAIN ACYL-COA DEHYDROGENASE DEFICIENCY
Phase: PHASE2 • Sponsor: Jerry Vockley, MD, PhD • Aim: Disease control
Last updated May 26, 2026 08:47 UTC
-
Could a fatty acid drug stop dangerous sugar drops in rare disease?
Prevention TerminatedThis study tests a drug called triheptanoin in 8 adults with MCADD, a rare genetic condition that can cause dangerously low blood sugar. The drug is already approved for a similar disorder. Researchers want to see if it is safe and can prevent hypoglycemia during fasting. Partici…
Matched conditions: MEDIUM-CHAIN ACYL-COA DEHYDROGENASE DEFICIENCY
Phase: PHASE2 • Sponsor: Jerry Vockley, MD, PhD • Aim: Prevention
Last updated May 26, 2026 08:32 UTC