Limb girdle muscular dystrophy type 2D/R3

Clinical trials for Limb girdle muscular dystrophy type 2D/R3 explained in plain language.

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Terminated 1

Experimental gene therapy tested for rare muscular dystrophy

Disease control Stopped early

This early-stage trial tested a gene therapy called SRP-9004 in just 4 people with limb girdle muscular dystrophy type 2D/R3, a rare muscle-weakening disease. The main goal was to check safety, not effectiveness. The study was terminated early, so results are limited.

Matched conditions: LIMB GIRDLE MUSCULAR DYSTROPHY TYPE 2D/R3

Phase 1 • Sponsor: Sarepta Therapeutics, Inc. • Aim: Disease control

Last updated Jun 26, 2026 13:47 UTC

Limb girdle muscular dystrophy type 2D/R3

Get alerted when new Limb girdle muscular dystrophy type 2D/R3 trials appear

Experimental gene therapy tested for rare muscular dystrophy