LATE-ONSET POMPE DISEASE
Clinical trials for LATE-ONSET POMPE DISEASE explained in plain language.
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New pompe disease drug moves to first human tests
Disease control CompletedThis early-phase study tested a new drug called ABX1100 in 46 healthy volunteers and people with late-onset Pompe disease. The main goal was to check safety and how the drug moves through the body. Researchers gave single or multiple doses by IV and watched for side effects over …
Matched conditions: LATE-ONSET POMPE DISEASE
Phase: EARLY_PHASE1 • Sponsor: Aro Biotherapeutics • Aim: Disease control
Last updated May 11, 2026 20:49 UTC
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Breathing exercises show promise for pompe patients
Symptom relief CompletedThis study tested a high-dose breathing muscle training program for people with late-onset Pompe disease, a condition that weakens muscles including those used for breathing. The training was done at home using video visits and special devices. The goal was to see if it was safe …
Matched conditions: LATE-ONSET POMPE DISEASE
Phase: NA • Sponsor: Duke University • Aim: Symptom relief
Last updated May 26, 2026 04:17 UTC