HUNTER SYNDROME
Clinical trials for HUNTER SYNDROME explained in plain language.
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Hunter syndrome immune study pulled before it started
Disease control TerminatedThis study aimed to see if a combination of drugs could stop the body from attacking a standard Hunter syndrome therapy (ELAPRASE). It was designed for boys who had never received ELAPRASE and were at risk for harmful antibodies. However, the study was withdrawn before any partic…
Matched conditions: HUNTER SYNDROME
Phase: PHASE4 • Sponsor: Takeda • Aim: Disease control
Last updated May 26, 2026 12:09 UTC
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Hunter syndrome drug combo tested for Long-Term safety in kids and adults
Disease control OngoingThis study is a follow-up for people with Hunter syndrome and cognitive problems who already took part in earlier trials. It aims to check the long-term safety of two drugs given together: idursulfase-IT (injected into the spine) and Elaprase (given through a vein). About 6 child…
Matched conditions: HUNTER SYNDROME
Phase: PHASE2, PHASE3 • Sponsor: Takeda • Aim: Disease control
Last updated May 26, 2026 12:04 UTC
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New stem cell approach shows promise for rare childhood diseases
Disease control OngoingThis study tests a stem cell transplant method for people with inherited metabolic disorders and severe osteopetrosis. The goal is to see if a donor's stem cells can successfully take over the patient's bone marrow while keeping side effects low. Participants receive chemotherapy…
Matched conditions: HUNTER SYNDROME
Phase: PHASE2 • Sponsor: Masonic Cancer Center, University of Minnesota • Aim: Disease control
Last updated May 26, 2026 10:35 UTC