GAUCHER DISEASE, TYPE 1
Clinical trials for GAUCHER DISEASE, TYPE 1 explained in plain language.
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New hope for gaucher patients: first human trial of FLT201
Disease control CompletedThis early-stage study tested a new treatment called FLT201 in 6 adults with Gaucher disease type 1. The goal was to see if it is safe and can boost the missing enzyme that causes the disease. Researchers hope this approach may reduce harmful buildup in cells and improve symptoms…
Matched conditions: GAUCHER DISEASE, TYPE 1
Phase: PHASE1 • Sponsor: Spur Therapeutics • Aim: Disease control
Last updated May 22, 2026 13:55 UTC
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Gaucher disease study probes brain chemistry for clues
Knowledge-focused CompletedThis study measured levels of certain brain and blood chemicals linked to oxidative stress and inflammation in people with Gaucher disease type 1 and healthy volunteers. The goal was to see if these chemicals are different in Gaucher patients. 33 adults took part, and the study u…
Matched conditions: GAUCHER DISEASE, TYPE 1
Phase: PHASE2 • Sponsor: University of Minnesota • Aim: Knowledge-focused
Last updated May 22, 2026 14:02 UTC