Retinitis pigmentosa 4
MONDO:0013395Any retinitis pigmentosa in which the cause of the disease is a mutation in the RHO gene.
Also known as: RHO retinitis pigmentosa, RP4, retinitis pigmentosa 4, retinitis pigmentosa 4, autosomal dominant or recessive, retinitis pigmentosa caused by mutation in RHO, retinitis pigmentosa type 4, RP 4, retinitis pigmentosa, rhodopsin-related
30 clinical trials for this condition and its sub-types, 5 tagged with Retinitis pigmentosa 4 itself.
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Can a single eye injection restore sight in genetic blindness?
Cure OngoingThis trial tests an experimental gene therapy called OCU400 in people with retinitis pigmentosa or Leber congenital amaurosis, which are inherited conditions that cause progressive vision loss and can lead to blindness. The therapy is given as a single injection into the eye, wit…
Phase 1/2 • Sponsor: Ocugen • Aim: Cure
Last updated Aug 02, 2026 00:00 UTC
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Gene therapy trial aims to restore night vision in rare eye disease
Disease control OngoingThis study tests a gene therapy called OCU400 for people with retinitis pigmentosa, an inherited eye disease that causes vision loss. The treatment is injected under the retina to help light-sensitive cells work better. The trial enrolled 140 people aged 3 and older and measures …
Phase 3 • Sponsor: Ocugen • Aim: Disease control
Last updated Aug 02, 2026 00:00 UTC