Retinitis pigmentosa 11
MONDO:0010828Any retinitis pigmentosa in which the cause of the disease is a mutation in the PRPF31 gene.
Also known as: PRPF31 retinitis pigmentosa, RP11, retinitis pigmentosa 11, retinitis pigmentosa caused by mutation in PRPF31, retinitis pigmentosa type 11, RP 11
29 clinical trials for this condition and its sub-types, 4 tagged with Retinitis pigmentosa 11 itself.
Follow this condition to get notified about new trialsWhere it sits in the disease tree
Browse by category →-
New eye injection shows promise for rare Blindness-Causing gene mutation
Disease control CompletedThis early-stage study tested the safety of a new drug called VP-001, given as an injection into the eye, for people with a rare genetic eye disease (PRPF31 mutation) that causes vision loss. Six participants aged 12 and older received multiple doses. The main goal was to check f…
Phase 1 • Sponsor: PYC Therapeutics • Aim: Disease control
Last updated Jun 27, 2026 13:00 UTC
-
New eye injection shows promise for rare Blindness-Causing gene mutation
Disease control CompletedThis early-stage study tested a new drug, VP-001, given as an injection into the eye to see if it is safe for people with a rare genetic eye disease caused by a PRPF31 mutation. Seventeen adults took part. The main goal was to check for side effects, not to measure vision improve…
Phase 1 • Sponsor: PYC Therapeutics • Aim: Disease control
Last updated Jun 27, 2026 13:00 UTC