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Optic atrophy 8

MONDO:0024569

Also known as: OPA8, optic atrophy 8

17 clinical trials for this condition and its sub-types, 0 tagged with Optic atrophy 8 itself.

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Where it sits in the disease tree

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Part of

↑ Autosomal dominant optic atrophy plus syndrome (0)

Including sub-types (17) Tagged with Optic atrophy 8 (0)

Trials to join now! 8 Not yet recruiting 1 Not yet finished but already full! 5 Completed 2 Terminated 1

New drug aims to tame hard-to-control seizures in rare mitochondrial disorders

Disease control Stopped early

This study tested a drug called vatiquinone in 68 people with mitochondrial disease and epilepsy that doesn't respond to standard treatments. Participants were randomly assigned to receive either vatiquinone or a placebo for 24 weeks to see if the drug could reduce the number of …

Phase 2/3 • Sponsor: PTC Therapeutics • Aim: Disease control

Last updated Jun 27, 2026 12:03 UTC