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Amyotrophic lateral sclerosis type 1
MONDO:0007103Also known as: ALS1, amyotrophic lateral sclerosis 1, amyotrophic lateral sclerosis type 1, FALS, amyotrophic lateral sclerosis 1, autosomal dominant, amyotrophic lateral sclerosis 1, autosomal dominant amyotrophic lateral sclerosis 1, autosomal recessive, included, amyotrophic lateral sclerosis 1, autosomal recessive, amyotrophic lateral sclerosis 1, familial
18 clinical trials for this condition and its sub-types, 8 tagged with Amyotrophic lateral sclerosis type 1 itself.
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New hope for ALS: first human trial of Gene-Targeting drug begins
Disease control Recruiting nowThis study tests an experimental drug called ALN-SOD in people with ALS caused by a mutation in the SOD1 gene. The drug is given via spinal injection to target the root cause of the disease. The main goal is to check safety, but researchers will also measure effects on biomarkers…
Phase 1/2 • Sponsor: Regeneron Pharmaceuticals • Aim: Disease control
Last updated Sep 13, 2026 00:00 UTC
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New study tracks safety of ALS drug tofersen over 7 years
Knowledge-focused Recruiting nowThis study looks at the long-term safety of the drug tofersen (Qalsody®) in people with a rare, inherited form of ALS called SOD1-ALS. Researchers will collect health information from about 125 participants in Europe and the US over at least 7 years. The main goal is to see what …
Sponsor: Biogen • Aim: Knowledge-focused
Last updated Jun 27, 2026 12:05 UTC