New hope for kids with rare bleeding disorder

NCT ID NCT05582993

Summary

This study is testing whether a lab-made clotting factor called vonicog alfa can safely prevent bleeding episodes in children with severe Von Willebrand Disease (VWD). It will enroll 24 children under 18 who have previously been treated for VWD. Participants will receive the treatment for 12 months to see if it reduces their annual bleeding rate compared to their past treatments.

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Azienda Ospedaliera Pediatrica Santobono Pausillipon

    RECRUITING

    Naples, 80123, Italy

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Azienda Ospedaliero-Universitaria Città della Salute e della Scienza di Torino

    RECRUITING

    Turin (Torino), 10126, Italy

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Bleeding and Clotting Disorders Institute

    RECRUITING

    Peoria, Illinois, 61614, United States

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Children's Health Care d/b/a Children's Minnesota

    RECRUITING

    Minneapolis, Minnesota, 55404, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Children's Health Ireland

    RECRUITING

    Dublin, D12N512, Ireland

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Childrens Hospital of Michigan

    RECRUITING

    Detroit, Michigan, 48201, United States

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Hemostase Clinique - Institut Cœur-Poumons (4eme étage aile est) Bureau 419

    RECRUITING

    Lille, 59037, France

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • Hopital Edouard Herriot - CHU Lyon

    RECRUITING

    Lyon, 69677, France

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Medical University of South Carolina (MUSC)

    RECRUITING

    Charleston, South Carolina, 29425, United States

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Nara Medical University Hospital

    RECRUITING

    Kashihara, 634-8522, Japan

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • New York - Presbyterian/Weill Cornell Medical Center

    RECRUITING

    New York, New York, 10021, United States

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Riley Hospital for Children Indiana University Health

    RECRUITING

    Indianapolis, Indiana, 46202, United States

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • Rutgers - Robert Wood Johnson Medical School

    RECRUITING

    New Brunswick, New Jersey, 08901, United States

    Contact Phone: •••-•••-•••• Email: •••••@•••••

    Contact

  • University of Alabama at Birmingham

    RECRUITING

    Birmingham, Alabama, 35223, United States

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

  • University of Iowa Hospitals & Clinics PARENT

    RECRUITING

    Iowa City, Iowa, 52242, United States

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.