Vitamin compound tested for rare brain disease PKAN
NCT ID NCT04182763
First seen Nov 01, 2025 · Last updated May 23, 2026 · Updated 30 times
Summary
This study tested a vitamin metabolite in 77 people with PKAN, a rare genetic disorder that affects movement and brain function. The main goal was to see if the study product is safe and tolerable, and to measure any changes in the disease. Researchers also looked at gene expression to understand how the body processes the product.
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Locations
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Oregon Health & Science University
Portland, Oregon, 97239, United States
Conditions
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