Vitamin compound studied for rare brain disease PKAN

NCT ID NCT04182763

First seen Jun 27, 2026 · Last updated Jun 27, 2026

Summary

This study looked at how people with PKAN, a rare genetic brain disorder, respond to a special vitamin metabolite. Researchers wanted to see if it is safe and if it changes any signs of the disease. 77 people aged 3 months to 89 years took part.

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Conditions

The condition(s) this trial relates to.

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Oregon Health & Science University

    Portland, Oregon, 97239, United States