New gene therapy aims to halt vision loss in rare eye disease

NCT ID NCT07002398

First seen Jan 04, 2026 · Last updated May 13, 2026 · Updated 26 times

Summary

This early-stage trial tests a gene therapy called VG801 for people with Stargardt disease, an inherited condition that causes progressive vision loss. The study will enroll 15 participants aged 6 and older who have confirmed ABCA4 gene mutations and poor vision in one eye. The goal is to check the safety of the treatment and see if it can help slow or stop further vision decline.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Shanghai General Hospital

    RECRUITING

    Shanghai, Shanghai Municipality, 200080, China

    Contact Phone: •••-•••-••••

    Contact

Conditions

Explore the condition pages connected to this study.