New hope for kids with stubborn histiocytosis: vemurafenib dose trial launched

NCT ID NCT04943198

First seen Apr 10, 2026 · Last updated May 15, 2026 · Updated 6 times

Summary

This study is for children with a rare disease called histiocytosis that has not improved with standard treatments and who have a specific gene change (BRAF mutation). The goal is to find the best dose and timing of the drug vemurafenib to control the disease. About 25 children will take part, and researchers will track how long they stay free of disease worsening or relapse.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Mother and Child Institute

    RECRUITING

    Warsaw, Mazovian, 01-211, Poland

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.