New hope for boys with Muscle-Wasting disease: safer steroid shows promise

NCT ID NCT05185622

Summary

This study tested vamorolone, a new type of steroid medication, in boys with Duchenne muscular dystrophy (DMD). It aimed to see if the drug was safe and how the body processed it, while also looking for early signs of benefit. The trial included 54 boys, aged 2-4 and 7-18, who took the drug daily for 12 weeks.

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Contacts and locations

Locations

  • Alberta's Children Hospital

    Calgary, Alberta, AB T3B 6A8, Canada

  • British Columbia Children's Hospital

    Vancouver, British Columbia, V6H 3N1, Canada

  • Children's Hospital of Eastern Ontario

    Ottawa, Ontario, K1H 8L1, Canada

  • Montreal Childrens Hospital

    Montreal, H4A 3J1, Canada

  • The Hospital for Sick Children

    Toronto, Ontario, M5G 1X8, Canada

Conditions

Explore the condition pages connected to this study.