Lifeline extended for boys with Muscle-Wasting disease
Disease control
AVAILABLE
This program provides continued access to the drug vamorolone for boys with Duchenne muscular dystrophy (DMD) who have already taken it in previous clinical studies. It allows them to keep receiving the medication while it is being reviewed for full market approval. The goal is t…
Sponsor: Santhera Pharmaceuticals • Aim: Disease control
Last updated Apr 02, 2026 02:11 UTC