New hope for kids with tough neuroblastoma? trial tests stronger therapies

NCT ID NCT03165292

First seen Jun 26, 2026 · Last updated Jun 26, 2026

Summary

This phase 2 trial tested two stronger treatment plans for children with very high risk neuroblastoma whose cancer did not respond well to initial chemotherapy. The treatments combined radioactive therapy (mIBG), chemotherapy drugs (topotecan and thiotepa), and a stem cell transplant. The goal was to see if these intensified approaches could improve survival. However, the trial was terminated early after enrolling only 34 participants, so the results are limited.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

mIBG (radioactive iodine), topotecan, thiotepa, and autologous stem cell transplant

What this could lead to

If successful, this could offer a more effective treatment option for children with very high risk neuroblastoma who have a poor response to initial chemotherapy.

What could go wrong

This trial was terminated early with only 34 participants, so results are limited. The treatments involve high-dose chemotherapy and radiation, which carry significant side effects.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

neuroblastoma

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Fondazione IRCCS Istituto nazionaleTumori

    Milan, 20133, Italy

  • Gustave Roussy

    Villejuif, Val De Marne, 94805, France

  • Hospital Universitario Cruces

    Cruces, 48903, Spain

  • Hospital Universitario y policnico La Fe

    Valencia, 46026, Spain

  • Medizinische Universität Innsbruck

    Innsbruck, 356020, Austria

  • Meyer children's Hospita

    Florence, 50139, Italy

  • Ospedale Pediatrico Bambino Gesù

    Roma, Italy

  • Princess Maxima Center

    Utrecht, Netherlands

  • St. Anna Kinderspital GmbH

    Vienna, 1090, Austria