New hope for kids with rare blood disease: trametinib trial opens

NCT ID NCT04943224

First seen Mar 28, 2026 · Last updated May 13, 2026 · Updated 8 times

Summary

This study is for children with a rare blood disorder called histiocytosis that hasn't responded to standard treatments. It tests different doses and timing of the drug trametinib to find the best way to control the disease. The goal is to improve how long children stay free of cancer progression or relapse.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Mother and Child Institute

    RECRUITING

    Warsaw, Mazovian, 01-211, Poland

    Contact

    Contact Phone: •••-•••-•••• Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.