Drug combo aims at genetic weaknesses in head and neck cancer

NCT ID NCT04997902

First seen Jun 27, 2026 · Last updated Jun 27, 2026

Summary

This early-stage trial tested a combination of two oral drugs, tipifarnib and alpelisib, in 45 adults with recurrent or metastatic head and neck squamous cell carcinoma that has specific genetic changes (HRAS overexpression or PIK3CA mutations). The goal was to find a safe dose and see if the drugs can shrink tumors. The study is now complete, and results will help guide future research.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

tipifarnib and alpelisib (oral drugs)

What this could lead to

If successful, this combination could offer a new treatment option for people with advanced head and neck cancer that has specific genetic changes.

What could go wrong

This is an early-phase trial with only 45 participants, so results may not apply broadly. The drugs can cause side effects, and the combination may not shrink tumors effectively.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

Head and Neck Neoplasms head and neck squamous cell carcinoma hereditary sensory and autonomic neuropathy Recurrence Squamous Cell Carcinoma of Head and Neck

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • City of Hope Comprehensive Cancer Center

    Duarte, California, 91010, United States

  • Dana-Farber Cancer Institute (Head and Neck Cancer Treatment Center)

    Boston, Massachusetts, 02215, United States

  • Johns Hopkins University School of Medicine (Sidney Kimmel Comprehensive Cancer Center)

    Baltimore, Maryland, 21231, United States

  • Lake Nona DDU (Florida Cancer Specialists)

    Orlando, Florida, 32827, United States

  • Memorial Sloan Kettering Cancer Center

    New York, New York, 10065, United States

  • UPMC Hillman Cancer Center

    Pittsburgh, Pennsylvania, 15232, United States

  • UT Southwestern Medical Center (Harold C. Simmons Comprehensive Cancer Center)

    Dallas, Texas, 75390, United States

  • University of Maryland School of Medicine (Marlene and Stewart Greenebaum Comprehensive Cancer Center)

    Baltimore, Maryland, 21201, United States

  • University of Texas MD Anderson Cancer Center

    Houston, Texas, 77030, United States

  • University of Wisconsin Carbone Cancer Center

    Madison, Wisconsin, 53792, United States

  • Washington University, School of Medicine

    St Louis, Missouri, 63110, United States