Testing an implanted port to deliver SMA medication

NCT ID NCT06555419

Summary

This study aims to understand how the body processes the SMA drug nusinersen when it's delivered through a new implanted port system called ThecaFlex DRx, compared to the standard spinal injection method. The research involves about 58 people with Spinal Muscular Atrophy who are already receiving regular nusinersen treatment. Participants will receive the drug both ways, and researchers will measure drug levels in their blood over 24 hours to compare the two delivery methods.

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Contacts and locations

Study contacts

  • Contact

    Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Ann & Robert H. Lurie Children's Hospital of Chicago

    RECRUITING

    Chicago, Illinois, 60611-2605, United States

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  • Boston Children's Hospital

    RECRUITING

    Boston, Massachusetts, 02115, United States

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  • Children's Hospital of Orange County

    RECRUITING

    Orange, California, 92868, United States

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  • Children's Hospital of Philadelphia

    RECRUITING

    Philadelphia, Pennsylvania, 19104, United States

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  • Children's Hospital of the King's Daughters_Norfolk

    RECRUITING

    Norfolk, Virginia, 23507, United States

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  • Fondazione Policlinico Universitario Agostino Gemelli IRCCS

    WITHDRAWN

    Roma, 168, Italy

  • Fondazione Serena Onlus - Centro Clinico Nemo_Milano

    WITHDRAWN

    Milan, 20162, Italy

  • Helen DeVos Children's Hospita

    RECRUITING

    Grand Rapids, Michigan, 49503, United States

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  • Hospital Universitari i Politecnic La Fe_Valencia

    RECRUITING

    Valencia, 46026, Spain

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  • Hospital Universitario La Paz

    RECRUITING

    Madrid, 28046, Spain

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  • Hôpital Raymond Poincaré

    RECRUITING

    Garches, Hauts De Seine, 92380, France

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  • Instytut Centrum Zdrowia Matki Polki

    NOT_YET_RECRUITING

    Lodz, 93-338, Poland

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  • Milton S. Hershey Medical Center | Pennsylvania State University_Hershey

    RECRUITING

    Hershey, Pennsylvania, 17033, United States

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  • Royal Hallamshire Hospital Neurology Department

    RECRUITING

    Sheffield, South Yorkshire, S102JF, United Kingdom

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  • Stacey Hall Developmental Pediatrics

    RECRUITING

    Charlottesville, Virginia, 22903, United States

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  • Stanford University Medical Center | Department of Neurology_Palo Alto

    RECRUITING

    Palo Alto, California, 94304, United States

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  • Szpital Specjalistyczny im. L.Rydygiera w Krakowie

    NOT_YET_RECRUITING

    Krakow, 31-826, Poland

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  • Texas Childrens Hospital Houston

    RECRUITING

    Houston, Texas, 77030, United States

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  • Universitaetsklinikum Essen

    RECRUITING

    Essen, 45147, Germany

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Conditions

Explore the condition pages connected to this study.