New drug shows promise in controlling rare blood clot disease

NCT ID NCT04683003

First seen Apr 07, 2026 · Last updated May 07, 2026 · Updated 5 times

Summary

This study looks at the long-term safety of a medicine called TAK-755 for people with a rare inherited condition that causes dangerous blood clots and bleeding. Participants receive the drug regularly to prevent flare-ups or as needed to treat them. The goal is to see if long-term use is safe and helps control the disease.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

Get updates

Get notified about this study

Sign up to get updates when this study changes or when new studies for THROMBOTIC THROMBOCYTOPENIC PURPURA (TTP) are added.

Our safety recommendation!

By submitting, you agree to our Terms of use

Contacts and locations

Locations

  • AKH - Medizinische Universität Wien

    Vienna, 1090, Austria

  • Azienda Socio Sanitaria Territoriale Papa Giovanni XXIII (Presidio Papa Giovanni XXIII)

    Bergamo, Hubei, 24127, Italy

  • Beijing Children's Hospital

    Beijing, Beijing Municipality, 100045, China

  • CHU Saint Etienne - Hôpital Nord

    Saint-Priest-en-Jarez Cedex, Pays de la Loire Region, 42270, France

  • Childrens Healthcare of Atlanta

    Atlanta, Georgia, 30322, United States

  • Complejo Hospitalario Universitario A Coruña

    A Coruña, La Coruña, 15006, Spain

  • Duke University Medical Center

    Durham, North Carolina, 27705, United States

  • Hospital de Cruces

    Barakaldo, Vizcaya, 48903, Spain

  • Hyogo College of Medicine Hospital

    Nishinomiya, Hyōgo, 663-8501, Japan

  • Hôpital Necker - Enfants Malades

    Paris, Paris, 75015, France

  • Hôpital Robert Debré- Paris

    Paris, 75935, France

  • Hôpital Saint-Antoine

    Paris, 75012, France

  • Inselspital -Universitaetsspital Bern

    Bern, 3010, Switzerland

  • Institute of Hematology and Hospital of Blood Disease

    Tianjin, Tianjin Municipality, 300021, China

  • Instytut Hematologii i Transfuzjologii

    Warsaw, 02-776, Poland

  • Kyushu University Hospital

    Fukuoka, Fukuoka, 812-8582, Japan

  • Medical Hospital,Tokyo Medical and Dental University

    Bunkyo City, Tokyo, 113-8519, Japan

  • Mid Ohio Heart Clinic Inc

    Dublin, Ohio, 43017, United States

  • Peking Union Medical College Hospital

    Beijing, Beijing Municipality, 100730, China

  • Roswell Park Comprehensive Cancer Center

    Buffalo, New York, 14203, United States

  • Samodzielny Publiczny Dzieciecy Szpital Kliniczny

    Warsaw, 02-091, Poland

  • The First Affiliated Hospital of Soochow University

    Suzhou, Jiangsushe, 215006, China

  • Tongji Hospital Affiliated to Tongji Medicine University

    Wuhan, Hubei, 430030, China

  • Universitaetsklinikum Hamburg-Eppendorf

    Hamburg, 20246, Germany

  • Universitaetsklinikum Jena, Klinik fuerKinder-und Jugendmedizin

    Jena, 07747, Germany

  • University College London Hospitals

    London, Greater London, NW12PG, United Kingdom

  • University of Oklahoma

    Oklahoma City, Oklahoma, 73104, United States

Conditions

Explore the condition pages connected to this study.