New drug hopes to strengthen muscles in rare genetic disorder
NCT ID NCT07560020
First seen Jun 27, 2026 · Last updated Jun 27, 2026
Summary
This study tests a medicine called surlorian in 28 adults with a rare genetic muscle disease (RYR1-related myopathy) that causes weakness. The goal is to see if surlorian improves muscle strength and function, like standing from a chair or walking. Participants will be randomly assigned to receive either surlorian or a placebo, and neither they nor the doctors will know which they get.
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the original study
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Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Conditions
The condition(s) this trial relates to.
As listed by the trial registrant
The condition terms exactly as the trial's registrant entered them.
Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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AP-HM- Hôpital de La Timone
Marseille, Bouches-du-Rhône, 13385, France
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Charité - Campus Berlin Buch
Berlin, State of Berlin, 13125, Germany
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Hospital Universitario Vall d'Hebron - PPDS
Barcelona, Barcelona, 8035, Spain
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Hospital Universitario de Donostia
San Sebastián, Guipúzcoa, 20014, Spain
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Institut de Myologie - Hôpital de La Pitié-Salpétrière
Paris, 73013, France
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Radboud Universitair Medisch Centrum
Nijmegen, Gelderland, 6500 HB, Netherlands
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The Robert Jones and Agnes Hunt Orthopaedic Hospital
Oswestry, Shropshire, SY10 7AG, United Kingdom
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University College Hospital - PPDS
London, WC1N 3BG, United Kingdom
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Universitätsklinikum Ulm
Ulm, Baden-Wurttemberg, 89081, Germany