New drug hopes to strengthen muscles in rare genetic disorder
Disease control
Not yet recruiting
This study tests a medicine called surlorian in 28 adults with a rare genetic muscle disease (RYR1-related myopathy) that causes weakness. The goal is to see if surlorian improves muscle strength and function, like standing from a chair or walking. Participants will be randomly a…
Phase: PHASE2 • Sponsor: RyCarma Therapeutics, Inc. • Aim: Disease control
Last updated Jun 27, 2026 12:26 UTC