New hope for a cure: gentler transplant aims to fix broken immune systems
NCT ID NCT04232085
Summary
This trial is testing a modified bone marrow transplant procedure designed to cure patients with rare, inherited disorders where the immune system or bone marrow doesn't work properly. The approach uses a less intense pre-transplant treatment and a specific drug after the transplant to help the patient's body accept the donor cells better and reduce dangerous side effects. The main goal is to see if this method leads to successful, long-term engraftment of the donor's healthy cells.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Johns Hopkins University
RECRUITINGBaltimore, Maryland, 21287, United States
Contact
Contact Email: •••••@•••••
Conditions
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