New hope for a cure: gentler transplant aims to fix broken immune systems

NCT ID NCT04232085

Summary

This trial is testing a modified bone marrow transplant procedure designed to cure patients with rare, inherited disorders where the immune system or bone marrow doesn't work properly. The approach uses a less intense pre-transplant treatment and a specific drug after the transplant to help the patient's body accept the donor cells better and reduce dangerous side effects. The main goal is to see if this method leads to successful, long-term engraftment of the donor's healthy cells.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Johns Hopkins University

    RECRUITING

    Baltimore, Maryland, 21287, United States

    Contact

    Contact Email: •••••@•••••

Conditions

Explore the condition pages connected to this study.