Gentler transplant offers hope for rare disease patients
NCT ID NCT04528355
Summary
This study is collecting information on a less intense stem cell transplant method for people with inherited disorders like immune deficiencies, sickle cell disease, or metabolic diseases. It aims to see how well patients recover, how often the transplant is successful, and how long they live after the procedure. The goal is to gather data to improve future treatments for these serious conditions.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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UPMC Children's Hospital of Pittsburgh
RECRUITINGPittsburgh, Pennsylvania, 15224, United States
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Contact
Contact Phone: •••-•••-•••• Email: •••••@•••••
Conditions
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