Gentler transplant offers hope for kids with rare, Life-Limiting diseases
NCT ID NCT01962415
Summary
This study is testing a less intense, potentially safer stem cell transplant procedure for children and young adults with serious inherited disorders like sickle cell disease, immune deficiencies, and metabolic diseases. The goal is to see if using lower doses of chemotherapy before the transplant can reduce severe side effects and organ damage while still allowing the donor cells to work. Researchers will track survival, recovery, and long-term health in about 100 participants.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
Locations
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UPMC Children's Hospital of Pittsburgh
RECRUITINGPittsburgh, Pennsylvania, 15224, United States
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Conditions
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