Gentler transplant offers hope for kids with rare blood diseases
NCT ID NCT00920972
Summary
This study is testing a less intense stem cell transplant procedure for children and young adults with inherited disorders like sickle cell disease and metabolic conditions. The goal is to replace a patient's faulty blood-forming system with a healthy donor's cells while reducing the severe side effects often seen with traditional transplants. Researchers will closely monitor if the donor cells successfully take hold and track the safety of the new approach.
This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes NO responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
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Contact
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Locations
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All Children's Hospital
COMPLETEDSt. Petersburg, Florida, 33701, United States
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BC Children's Hospital
COMPLETEDVancouver, British Columbia, V6H 3N1, Canada
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Carolinas Medical Center
COMPLETEDCharlotte, North Carolina, 28232, United States
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Children's Hospital of New Orleans
COMPLETEDNew Orleans, Louisiana, 70118, United States
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Children's Hospital of Orange County
RECRUITINGOrange, California, 92868, United States
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Children's Memorial Hospital
COMPLETEDChicago, Illinois, 60614, United States
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Children's Mercy
COMPLETEDKansas City, Missouri, 64108, United States
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Columbia University Medical Center
RECRUITINGNew York, New York, 10032, United States
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Cook Children's Hospital
COMPLETEDForth Worth, Texas, 76104, United States
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Duke Children's Hospital
COMPLETEDDurham, North Carolina, 27705, United States
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George Washington University School of Medicine
RECRUITINGWashington D.C., District of Columbia, 20010, United States
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Hackensack University Medical Center
COMPLETEDHackensack, New Jersey, 07601, United States
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Indiana University School of Medicine
RECRUITINGIndianapolis, Indiana, 46202, United States
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Miami Children's Hospital
COMPLETEDMiami, Florida, 33155, United States
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Nemours Children's Health
COMPLETEDJacksonville, Florida, 32207, United States
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Phoenix Children's Hospital
RECRUITINGPhoenix, Arizona, 85016, United States
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St. Louis University
RECRUITINGSt Louis, Missouri, 63104, United States
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Texas Transplant Institute
COMPLETEDSan Antonio, Texas, 78229, United States
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The University of Oklahoma
COMPLETEDOklahoma City, Oklahoma, 73104, United States
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University of Calgary
COMPLETEDCalgary, Canada
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University of California
RECRUITINGSan Diego, California, 92123, United States
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University of Manitoba
COMPLETEDWinnipeg, Manitoba, MB R3E 0T4, Canada
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University of Miami
RECRUITINGMiami, Florida, 33136, United States
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University of North Carolina
RECRUITINGChapel Hill, North Carolina, 27514, United States
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University of Pittsburg
COMPLETEDPittsburgh, Pennsylvania, 15224, United States
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University of Utah
RECRUITINGSalt Lake City, Utah, 84132, United States
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Washington University School of Medicine (in St. Louis)
RECRUITINGSt Louis, Missouri, 63110, United States
Contact Phone: •••-•••-•••• Email: •••••@•••••
Contact Phone: •••-•••-•••• Email: •••••@•••••
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Yale School of Medicine
RECRUITINGNew Haven, Connecticut, 06510, United States
Contact
Conditions
Explore the condition pages connected to this study.