Stem cell transplant trial offers hope for halting rare brain disease
NCT ID NCT04503213
Summary
This study aims to measure whether stem cell transplants can slow or stop the progression of CSF1R-related leukoencephalopathy, a rare genetic brain disease. Researchers will follow 20 adult patients who have the genetic mutation and are scheduled to receive a transplant. They'll track changes in thinking, movement, and brain scans over time to see if the treatment helps control the disease.
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Contacts and locations
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Locations
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Mayo Clinic in Florida
Jacksonville, Florida, 32224, United States
Conditions
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