Three-Drug cocktail aims to harvest stem cells for rare immune disease cure
NCT ID NCT03055247
Summary
This study is testing a new combination of three drugs (Ibuprofen, G-CSF, and Plerixafor) to see if it safely and effectively collects stem cells from the blood of adults with X-linked Chronic Granulomatous Disease (X-CGD). The goal is to gather enough healthy stem cells so they can later be genetically corrected and used in a future gene therapy treatment. This is a small, early-phase study focused on the collection process itself.
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Contacts and locations
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Study contacts
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Contact
Phone: •••-•••-•••• Email: •••••@•••••
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Phone: •••-•••-•••• Email: •••••@•••••
Locations
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Ospedale Pediatrico Bambino Gesù
RECRUITINGRome, Lazio, 00165, Italy
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Ospedale San Raffaele
RECRUITINGMilan, Lombardy, 20132, Italy
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Conditions
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