New drug shows promise for rare hormone disorder

NCT ID NCT03257462

First seen Jun 25, 2026 · Last updated Jun 27, 2026 · Updated 1 time

Summary

This phase 2 trial tested a new drug called SPR001 in 24 adults with classic congenital adrenal hyperplasia (CAH), a genetic condition that disrupts hormone production. The study aimed to see if SPR001 is safe and can improve hormone control. Participants took multiple doses of the drug, and researchers measured changes in key hormones like 17-hydroxyprogesterone. The results could point toward a better way to manage this lifelong condition.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

SPR001 capsules

What this could lead to

If successful, SPR001 could offer a new way to better control hormone levels in people with classic congenital adrenal hyperplasia, potentially reducing symptoms and the need for high-dose steroids.

What could go wrong

This is a small, early-phase trial with only 24 participants. The drug may not show enough benefit or could have side effects. More research is needed before it could become a treatment.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

classic congenital adrenal hyperplasia due to 21-hydroxylase deficiency congenital adrenal hyperplasia

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Spruce Biosciences Clinical Site

    Orange, California, 92123, United States

  • Spruce Biosciences Clinical Site

    San Diego, California, 92123, United States

  • Spruce Biosciences Clinical Site

    Melbourne, Florida, 32935, United States

  • Spruce Biosciences Clinical Site

    Atlanta, Georgia, 30046, United States

  • Spruce Biosciences Clinical Site

    Indianapolis, Indiana, 46202, United States

  • Spruce Biosciences Clinical Site

    Ann Arbor, Michigan, 48109, United States

  • Spruce Biosciences Clinical Site

    Minneapolis, Minnesota, 55414, United States

  • Spruce Biosciences Clinical Site

    Las Vegas, Nevada, 89148, United States

  • Spruce Biosciences Clinical Site

    Philadelphia, Pennsylvania, 19104, United States