Gene therapy trial hopes to tame severe bleeding disorder

NCT ID NCT07226206

First seen Nov 10, 2025 · Last updated May 05, 2026 · Updated 26 times

Summary

This study is testing a new gene therapy called SPK-8011QQ in 5 adult men with severe or moderately severe hemophilia A, a condition where blood doesn't clot properly. The main goal is to see if the treatment is safe and tolerable. Researchers will monitor for side effects and lab changes, aiming to reduce bleeding risks.

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This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Contacts and locations

Study contacts

  • Contact

    Phone: •••-•••-•••• Email: •••••@•••••

Locations

  • Center for Inherited Blood Disorders

    RECRUITING

    Orange, California, 92868-4748, United States

  • Kaiser Permanente

    RECRUITING

    Vallejo, California, 94589-2441, United States

Conditions

Explore the condition pages connected to this study.