Could a cocktail of three drugs tame a rare paralyzing disease?

NCT ID NCT02314208

First seen Jun 26, 2026 · Last updated Jun 26, 2026 · Updated 1 time

Summary

This phase 2 trial tested three drugs—Xenbilox, Tahor, and resveratrol—in 12 adults with SPG5, a rare genetic condition causing progressive leg weakness. The goal was to lower levels of a toxic cholesterol byproduct called 27-hydroxycholesterol. Each drug was taken for 2 months, and blood levels were measured before and after treatment.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance
Xenbilox (chenodeoxycholic acid), Tahor (atorvastatin), and resveratrol
What this could lead to
If successful, this could point toward a treatment to slow or manage SPG5 by reducing toxic oxysterol buildup.
What could go wrong
This is a small, early-phase trial with only 12 participants, so results may not apply to everyone. The drugs may not effectively lower oxysterols or improve symptoms.

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Conditions

The condition(s) this trial relates to.

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Pitié-Salpêtrière Hospital

    Paris, France

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