Could a cocktail of three drugs tame a rare paralyzing disease?

NCT ID NCT02314208

First seen Jun 26, 2026 · Last updated Jun 26, 2026 · Updated 1 time

Summary

This phase 2 trial tested three drugs—Xenbilox, Tahor, and resveratrol—in 12 adults with SPG5, a rare genetic condition causing progressive leg weakness. The goal was to lower levels of a toxic cholesterol byproduct called 27-hydroxycholesterol. Each drug was taken for 2 months, and blood levels were measured before and after treatment.

What this could mean

Our plain-language read of the trial. This is informational only — not medical advice or a prediction.

Active substance

Xenbilox (chenodeoxycholic acid), Tahor (atorvastatin), and resveratrol

What this could lead to

If successful, this could point toward a treatment to slow or manage SPG5 by reducing toxic oxysterol buildup.

What could go wrong

This is a small, early-phase trial with only 12 participants, so results may not apply to everyone. The drugs may not effectively lower oxysterols or improve symptoms.

Disclaimer Read more

This is a summary of the original study . Summaries may miss details or leave out important information. Before applying or accepting participation, make sure you have read and understood the full study. Curemydisease.com takes no responsibility whatsoever for anything missed, misunderstood, or acted upon as a result of our summary — we know it does not capture everything.

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Conditions

The condition(s) this trial relates to.

hereditary spastic paraplegia hereditary spastic paraplegia 5A paraplegia

As listed by the trial registrant

The condition terms exactly as the trial's registrant entered them.

Contacts and locations

Locations

  • Pitié-Salpêtrière Hospital

    Paris, France